Research Categories: Research publications

Smith-Kingsmore syndrome caused by MTOR gene variation: 2 cases and literature review

January 18, 2024

[Smith-Kingsmore syndrome caused by MTOR gene variation: 2 cases and literature review]. Lei HH, Liu LL, Wang XL, Tie XC, Tian N, Ji Y, Yang Y. Zhonghua Er Ke Za...

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Smith-Kingsmore syndrome: A third family with the MTOR mutation c.5395G>A p.(Glu1799Lys)

January 18, 2024

Smith-Kingsmore syndrome: A third family with the MTOR mutation c.5395G>A p.(Glu1799Lys) and evidence for paternal gonadal mosaicism. Moosa S, Böhrer-Rabel H, Altmüller J, Beleggia F, Nürnberg P, Li Y, Yigit...

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A new case of Smith-Kingsmore syndrome with somatic MTOR

January 18, 2024

A new case of Smith-Kingsmore syndrome with somatic MTOR pathogenic variant expands the phenotypic spectrum to lateralized overgrowth. Carli D, Ferrero GB, Fusillo A, Coppo P, La Selva R, Zinali...

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Brain Tissue Low-Level Mosaicism for MTOR Mutation Causes Smith-Kingsmore Phenotype

January 18, 2024

Brain Tissue Low-Level Mosaicism for MTOR Mutation Causes Smith-Kingsmore Phenotype with Recurrent Hypoglycemia-A Novel Phenotype and a Further Proof for Testing of an Affected Tissue. Szczałuba K, Rydzanicz M, Walczak...

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A novel de novo MTOR gain-of-function variant in a patient with Smith-Kingsmore syndrome and Antiphospholipid syndrome.

January 18, 2024

A novel de novo MTOR gain-of-function variant in a patient with Smith-Kingsmore syndrome and Antiphospholipid syndrome. Rodríguez-García ME, Cotrina-Vinagre FJ, Bellusci M, Martínez de Aragón A, Hernández-Sánchez L, Carnicero-Rodríguez P,...

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Sleep and Circadian Disturbances in Children With Neurodevelopmental Disorders

January 18, 2024

Sleep and Circadian Disturbances in Children With Neurodevelopmental Disorders. Tamir S, Dye TJ, Witt RM. Semin Pediatr Neurol. 2023 Dec;48:101090. doi: 10.1016/j.spen.2023.101090. Epub 2023 Oct 4.PMID: 38065637

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Expanding the phenotype of MTOR-related disorders and the Smith-Kingsmore syndrome.

January 18, 2024

Expanding the phenotype of MTOR-related disorders and the Smith-Kingsmore syndrome. Elizondo-Plazas A, Ibarra-Ramírez M, Garza-Báez A, Martínez-de-Villarreal LE. Neurol Genet. 2020 May 7;6(3):e432. doi: 10.1212/NXG.0000000000000432. eCollection 2020 Jun. PMID: 32494756

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mTOR mutations in Smith-Kingsmore syndrome

January 18, 2024

mTOR mutations in Smith-Kingsmore syndrome: Four additional patients and a review. Gordo G, Tenorio J, Arias P, Santos-Simarro F, García-Miñaur S, Moreno JC, Nevado J, Vallespin E, Rodriguez-Laguna L, de...

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Delineating the Smith-Kingsmore syndrome phenotype

January 18, 2024

Delineating the Smith-Kingsmore syndrome phenotype: Investigation of 16 patients with the MTOR c.5395G > A p.(Glu1799Lys) missense variant. Poole RL, Curry PDK, Marcinkute R, Brewer C, Coman D, Hobson E, Johnson D,...

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Functional and structural analyses

January 18, 2024

Functional and structural analyses of novel Smith-Kingsmore Syndrome-Associated MTOR variants reveal potential new mechanisms and predictors of pathogenicity. Besterman AD, Althoff T, Elfferich P, Gutierrez-Mejia I, Sadik J, Bernstein JA,...

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